The emerging clustered regularly interspaced short palindromic repeat (CRISPR)/CRISPR-associated system (Cas) gene-editing system represents a promising tool for genome manipulation.

Despite a national policy draft being put in place by the Central government, there’s a lack of awareness on the issue of rare diseases.

India has one of the largest number of rare disease patients in the world and has recently come with a draft policy on rare diseases. A panel consisting of experts in the rare disease space from India as well as globally renowned experts from academia, industry, patient groups, among others engages in a broad discussion and take stock of the state of rare diseases as well as the one year of the formulation of the Rare Disease Policy in India.